Current and future pharmacological treatment strategies in X-linked adrenoleukodystrophy (Q24618949)

X-linked adrenoleukodystrophy

Europe PubMed Central

title

Current and future pharmacological treatment strategies in X-linked adrenoleukodystrophy (English)

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1 reference

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Johannes Berger

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Aurora Pujol

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2

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Patrick Aubourg

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3

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Sonja Forss-Petter

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4

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language of work or name

English

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publication date

July 2010

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published in

Brain Pathology

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volume

20

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issue

4

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page(s)

845-56

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cites work

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

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28 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2967711

Late onset neurological phenotype of the X-ALD gene inactivation in mice: a mouse model for adrenomyeloneuropathy.

28 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2967711

Fibrate induction of the adrenoleukodystrophy-related gene (ABCD2): promoter analysis and role of the peroxisome proliferator-activated receptor PPARalpha

28 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2967711

Characterization of the Adrenoleukodystrophy-Related (ALDR, ABCD2) Gene Promoter: Inductibility by Retinoic Acid and Forskolin

28 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2967711

The four murine peroxisomal ABC-transporter genes differ in constitutive, inducible and developmental expression.

28 November 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=2967711

Clinical improvement of adrenoleukodystrophy following intravenous gammaglobulin therapy

28 November 2018

1 reference

12 December 2020

Progression of X-linked adrenoleukodystrophy under interferon-beta therapy

1 reference

12 December 2020

Lovastatin for X-linked adrenoleukodystrophy

1 reference

12 December 2020

Simvastatin does not normalize very long chain fatty acids in adrenoleukodystrophy mice

1 reference

12 December 2020

Therapeutic plasma exchange in treatment of adrenoleukodystrophy

1 reference

12 December 2020

Retroviral-mediated adrenoleukodystrophy-related gene transfer corrects very long chain fatty acid metabolism in adrenoleukodystrophy fibroblasts: implications for therapy

1 reference

12 December 2020

Adrenoleukodystrophy: incidence, new mutation rate, and results of extended family screening

1 reference

12 December 2020

A randomized controlled study of modified cobratoxin in adrenomyeloneuropathy

1 reference

12 December 2020

Toxic effects of X-linked adrenoleukodystrophy-associated, very long chain fatty acids on glial cells and neurons from rat hippocampus in culture

1 reference

12 December 2020

X-linked adrenoleukodystrophy phenotype is independent of ABCD2 genotype

1 reference

12 December 2020

Simvastatin and plasma very-long-chain fatty acids in X-linked adrenoleukodystrophy

1 reference

12 December 2020

Lovastatin therapy for X-linked adrenoleukodystrophy: clinical and biochemical observations on 12 patients

1 reference

12 December 2020

Adrenoleukodystrophy. Failure of immunosuppression to prevent neurological progression

1 reference

12 December 2020

Evidence that oxidative stress is increased in patients with X-linked adrenoleukodystrophy

1 reference

https://api.crossref.org/works/10.1111%2FJ.1750-3639.2010.00393.X

7 January 2021

inferred from DOI database lookup

Identifiers

DOI

10.1111/J.1750-3639.2010.00393.X

1 reference

4591353

4591353

1 reference

1 reference

1 reference