Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell Type Specific Gene Editing. (Q52431661)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:29668265%20AND%20SRC:MED&resulttype=core&format=json

23 March 2020

title

Receptor-Mediated Delivery of CRISPR-Cas9 Endonuclease for Cell-Type-Specific Gene Editing (English)

1 reference

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23 March 2020

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27

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23 March 2020

Romain Rouet

1

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23 March 2020

Alison Varghese

15

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23 March 2020

Ross C Wilson

24

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23 March 2020

19

Kaihong Zhou

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23 March 2020

author name string

Benjamin A Thuma

2

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23 March 2020

Marc D Roy

3

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23 March 2020

Nathanael G Lintner

4

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23 March 2020

David M Rubitski

5

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23 March 2020

James E Finley

6

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23 March 2020

Hanna M Wisniewska

7

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23 March 2020

Rima Mendonsa

8

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23 March 2020

Ariana Hirsh

9

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23 March 2020

Lorena de Oñate

10

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23 March 2020

Justin Bellenger

13

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23 March 2020

Xidong Feng

14

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23 March 2020

Boris A Chrunyk

16

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23 March 2020

Kevin D Hesp

18

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23 March 2020

Nannan Ma

20

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23 March 2020

Meihua Tu

21

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23 March 2020

Robert Dullea

22

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23 March 2020

Spiros Liras

25

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23 March 2020

Vincent Mascitti

26

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23 March 2020

Joan Compte Barrón

11

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23 March 2020

Thomas J McLellan

12

1 reference

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23 March 2020

Kris Borzilleri

17

1 reference

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23 March 2020

Kim F McClure

23

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23 March 2020

language of work or name

English

0 references

publication date

18 May 2018

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Journal of the American Chemical Society

23 March 2020

published in

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23 March 2020

volume

140

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23 March 2020

page(s)

6596-6603

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23 March 2020

issue

21

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Overcoming cellular barriers for RNA therapeutics

23 March 2020

cites work

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Cationic lipid-mediated delivery of proteins enables efficient protein-based genome editing in vitro and in vivo

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3 July 2018

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3 July 2018

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3 July 2018

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3 July 2018

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Binding of synthetic oligosaccharides to the hepatic Gal/GalNAc lectin. Dependence on fine structural features.

3 July 2018

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Structure-guided chemical modification of guide RNA enables potent non-viral in vivo genome editing.

3 July 2018

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Immunity to CRISPR Cas9 and Cas12a therapeutics

13 August 2018

1 reference

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Asialoglycoprotein receptor 1 mediates productive uptake of N-acetylgalactosamine-conjugated and unconjugated phosphorothioate antisense oligonucleotides into liver hepatocytes.

13 August 2018

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Efficient Liver Targeting by Polyvalent Display of a Compact Ligand for the Asialoglycoprotein Receptor.

13 August 2018

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A genome-editing strategy to treat β-hemoglobinopathies that recapitulates a mutation associated with a benign genetic condition.

13 August 2018

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Nanoparticle delivery of Cas9 ribonucleoprotein and donor DNA induces homology-directed DNA repair

13 August 2018

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Multivalent N-acetylgalactosamine-conjugated siRNA localizes in hepatocytes and elicits robust RNAi-mediated gene silencing

30 November 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/29668265

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Hepatocyte-specific delivery of siRNAs conjugated to novel non-nucleosidic trivalent N-acetylgalactosamine elicits robust gene silencing in vivo

1 reference

PubMed

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inferred from PubMed ID database lookup

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9 October 2022

https://opencitations.net/index/coci/api/v1/references/10.1021/JACS.8B01551

Identifiers

DOI

10.1021/JACS.8B01551

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:29668265%20AND%20SRC:MED&resulttype=core&format=json

23 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:29668265%20AND%20SRC:MED&resulttype=core&format=json

23 March 2020

1 reference