Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 (Q63811425)
Jump to navigation
Jump to search
clinical trial
| Language | Label | Description | Also known as |
|---|---|---|---|
| English | Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 |
clinical trial |
Statements
STR1VE (English)
0 references
Phase 3, Open-Label, Single-Arm, Single-Dose Gene Replacement Therapy Clinical Trial for Patients With Spinal Muscular Atrophy Type 1 With One or Two SMN2 Copies Delivering AVXS-101 by Intravenous Infusion (English)
0 references
24 October 2017
0 references
30 November 2019
0 references
20
0 references