Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. (Q51768443)
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scientific article published in March 2009
Language | Label | Description | Also known as |
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English | Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. |
scientific article published in March 2009 |
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Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease. (English)
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Marc Nicolino
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Barry Byrne
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J Edmund Wraith
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Nancy Leslie
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Hanna Mandel
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David R Freyer
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Georgianne L Arnold
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Eniko K Pivnick
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C J Ottinger
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Peter H Robinson
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John-Charles A Loo
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Martin Smitka
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Philip Jardine
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Luciano Tatò
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Brigitte Chabrol
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Shawn McCandless
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Shigemi Kimura
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L Mehta
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Deeksha Bali
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Alison Skrinar
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Claire Morgan
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Lakshmi Rangachari
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Deya Corzo
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Priya S Kishnani
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1 March 2009
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11
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210-219
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3
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Identifiers
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