Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6. (Q45571369)

14 December 2017

Efficient transduction of skeletal muscle using vectors based on adeno-associated virus serotype 6. (English)

1 reference

14 December 2017

0 references

7

A Dusty Miller

1 reference

14 December 2017

Michael J Blankinship

1

1 reference

14 December 2017

Paul Gregorevic

2

1 reference

14 December 2017

James M Allen

3

1 reference

14 December 2017

Scott Q Harper

4

1 reference

14 December 2017

Hollie Harper

5

1 reference

14 December 2017

Christine L Halbert

6

1 reference

14 December 2017

Jeffrey S Chamberlain

8

1 reference

14 December 2017

1 October 2004

1 reference

14 December 2017

1 reference

14 December 2017

10

1 reference

14 December 2017

671-678

1 reference

14 December 2017

4

1 reference

Characteristics and taxonomy of Parvoviridae

14 December 2017

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

The atomic structure of adeno-associated virus (AAV-2), a vector for human gene therapy.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Definition of a novel promoter for the major adenovirus-associated virus mRNA.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Concatemers of alternating plus and minus strands are intermediates in adenovirus-associated virus DNA synthesis

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Rolling hairpin model for replication of parvovirus and linear chromosomal DNA

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

The cryptic life style of adeno-associated virus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

ADENOVIRUS-ASSOCIATED DEFECTIVE VIRUS PARTICLES

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Site-specific integration by adeno-associated virus

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Nucleotide sequencing and generation of an infectious clone of adeno-associated virus 3.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Preclinical in vivo evaluation of pseudotyped adeno-associated virus vectors for liver gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Adeno-associated virus type 6 (AAV6) vectors mediate efficient transduction of airway epithelial cells in mouse lungs compared to that of AAV2 vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Stable restoration of the sarcoglycan complex in dystrophic muscle perfused with histamine and a recombinant adeno-associated viral vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Epidemiology of adenovirus-associated virus infection in a nursery population

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Progress in adeno-associated virus type 2 vector production: promises and prospects for clinical use.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

The packaging capacity of adeno-associated virus (AAV) and the potential for wild-type-plus AAV gene therapy vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Cross-packaging of a single adeno-associated virus (AAV) type 2 vector genome into multiple AAV serotypes enables transduction with broad specificity

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

The use of adeno-associated virus to circumvent the maturation-dependent viral transduction of muscle fibers

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Advances in Duchenne muscular dystrophy gene therapy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Optimized production of high-titer recombinant adeno-associated virus in roller bottles

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Transfer of full-length Dmd to the diaphragm muscle of Dmd(mdx/mdx) mice through systemic administration of plasmid DNA

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

A new method for recombinant adeno-associated virus vector delivery to murine diaphragm

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Efficiency and functional consequences of adenovirus-mediated in vivo gene transfer to normal and dystrophic (mdx) mouse diaphragm

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Differential short-term transduction efficiency of adult versus newborn mouse tissues by adenoviral recombinants.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Highly efficient EIAV-mediated in utero gene transfer and expression in the major muscle groups affected by Duchenne muscular dystrophy

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

The hopes and fears of in utero gene therapy for genetic disease--a review.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

A phase II, double-blind, randomized, placebo-controlled clinical trial of tgAAVCF using maxillary sinus delivery in patients with cystic fibrosis with antrostomies.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Repeated adeno-associated virus serotype 2 aerosol-mediated cystic fibrosis transmembrane regulator gene transfer to the lungs of patients with cystic fibrosis: a multicenter, double-blind, placebo-controlled trial

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Three myosin heavy chain isoforms in type 2 skeletal muscle fibres.

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

Separation of Two Types of Adeno-Associated Virus Particles Containing Complementary Polynucleotide Chains

7 January 2021

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

7 January 2021

Nucleotide sequence and organization of the adeno-associated virus 2 genome

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

7 January 2021

Integration of the adeno-associated virus genome into cellular DNA in latently infected human Detroit 6 cells

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

7 January 2021

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.07.016

7 January 2021

10.1016/J.YMTHE.2004.07.016

Identifiers

DOI

1 reference

14 December 2017

1 reference