Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter (Q45457148)

14 December 2017

title

Correction of glycogen storage disease type II by an adeno-associated virus vector containing a muscle-specific promoter (English)

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14 December 2017

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glycogen storage disease

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Baodong Sun

1

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14 December 2017

Haoyue Zhang

2

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14 December 2017

Luis M Franco

3

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Talmage Brown

4

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14 December 2017

Andrew Bird

5

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Ayn Schneider

6

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Dwight D Koeberl

7

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14 December 2017

publication date

1 June 2005

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14 December 2017

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14 December 2017

volume

11

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issue

6

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14 December 2017

page(s)

889-898

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Systemic correction of the muscle disorder glycogen storage disease type II after hepatic targeting of a modified adenovirus vector encoding human acid-alpha-glucosidase

14 December 2017

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inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1016/J.YMTHE.2005.01.012

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14 December 2017

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