Long-term correction of ornithine transcarbamylase deficiency by WPRE-mediated overexpression using a helper-dependent adenovirus (Q45036081)

8 December 2017

title

Long-term correction of ornithine transcarbamylase deficiency by WPRE-mediated overexpression using a helper-dependent adenovirus (English)

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8 December 2017

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Asad Mian

1

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8 December 2017

W Michael McCormack

2

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8 December 2017

Viraj Mane

3

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Soledad Kleppe

4

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8 December 2017

Philip Ng

5

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8 December 2017

Milton Finegold

6

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8 December 2017

William E O'Brien

7

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8 December 2017

John R Rodgers

8

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Arthur L Beaudet

9

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Brendan Lee

10

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publication date

1 September 2004

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8 December 2017

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8 December 2017

volume

10

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8 December 2017

issue

3

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8 December 2017

page(s)

492-499

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8 December 2017

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Hepatocyte gene therapy in a large animal: a neonatal bovine model of citrullinemia

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Patient selection may affect gene therapy success. Dominant negative effects observed for ornithine transcarbamylase in mouse and human hepatocytes

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Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer

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Use of a liver-specific promoter reduces immune response to the transgene in adenoviral vectors

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Progress toward gene therapy of Duchenne muscular dystrophy

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CRM1-dependent function of a cis-acting RNA export element

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Tissue-specific, developmental, hormonal, and dietary regulation of rat phosphoenolpyruvate carboxykinase-human growth hormone fusion genes in transgenic mice

7 January 2021

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Optimization of the helper-dependent adenovirus system for production and potency in vivo

7 January 2021

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Diagnostic value of orotic acid excretion in heritable disorders of the urea cycle and in hyperammonemia due to organic acidurias

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7 January 2021

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7 January 2021

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A helper-dependent adenovirus vector system: removal of helper virus by Cre-mediated excision of the viral packaging signal

7 January 2021

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Woodchuck hepatitis virus contains a tripartite posttranscriptional regulatory element.

7 January 2021

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Woodchuck hepatitis virus posttranscriptional regulatory element enhances expression of transgenes delivered by retroviral vectors.

7 January 2021

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https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.036

inferred from DOI database lookup

7 January 2021

based on heuristic

Role of viral antigens in destructive cellular immune responses to adenovirus vector-transduced cells in mouse lungs.

1 reference

https://api.crossref.org/works/10.1016%2FJ.YMTHE.2004.05.036

inferred from DOI database lookup

7 January 2021

based on heuristic

Identifiers

DOI

10.1016/J.YMTHE.2004.05.036

1 reference

8 December 2017

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