Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C. (Q44985264)

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Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C.
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    Treatment with miglustat reverses the lipid-trafficking defect in Niemann-Pick disease type C. (English)
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    Danielle te Vruchte
    Emyr Lloyd-Evans
    Gabriele Reinkensmeier
    Daniel J Sillence
    Luisa Fernandez-Guillen
    Raymond A Dwek
    Terry D Butters
    Timothy M Cox
    1 August 2004
    654-658

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