Ataluren (PTC124) induces cystic fibrosis transmembrane conductance regulator protein expression and activity in children with nonsense mutation cystic fibrosis (Q42973495)

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scientific article published on 9 July 2010
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Ataluren (PTC124) induces cystic fibrosis transmembrane conductance regulator protein expression and activity in children with nonsense mutation cystic fibrosis
scientific article published on 9 July 2010

    Statements

    Ataluren (PTC124) induces cystic fibrosis transmembrane conductance regulator protein expression and activity in children with nonsense mutation cystic fibrosis (English)
    Isabelle Sermet-Gaudelus
    Kris De Boeck
    Georges J Casimir
    Agnès Mogenet
    Delphine Roussel
    Janine Fritsch
    Laurence Hanssens
    Samit Hirawat
    Nilsen L Miller
    Scott Constantine
    Allen Reha
    Temitayo Ajayi
    Gary L Elfring
    Langdon L Miller
    9 July 2010
    1262-1272

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