Mucopolysaccharidosis-like phenotype in feline Sandhoff disease and partial correction after AAV gene therapy. (Q41740847)

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8 March 2020

title

Mucopolysaccharidosis-like phenotype in feline Sandhoff disease and partial correction after AAV gene therapy (English)

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8 March 2020

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8 March 2020

Thomas S Denney

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8 March 2020

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Nouha Salibi

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Heather L Gray-Edwards

1

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8 March 2020

Brandon L Brunson

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8 March 2020

Merrilee Holland

3

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Allison M Bradbury

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Victoria J McCurdy

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Patricia M Beadlescomb

7

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8 March 2020

Ashley N Randle

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Aime K Johnson

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Meredith L Voyles

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Ronald D Montgomery

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Diane U Wilson

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Judith A Hudson

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8 March 2020

Nancy R Cox

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8 March 2020

Henry J Baker

18

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8 March 2020

Miguel Sena-Esteves

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Douglas R Martin

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8 March 2020

Ronald J Beyers

11

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language of work or name

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8 May 2015

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Molecular Genetics and Metabolism

8 March 2020

published in

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8 March 2020

volume

116

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8 March 2020

issue

1-2

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8 March 2020

page(s)

80-87

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Comparative analysis of brain lipids in mice, cats, and humans with Sandhoff disease

8 March 2020

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10.1016/J.YMGME.2015.05.003

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release_2degi4kjwzbklciva22njzktou

8 March 2020

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