Lessons learned from the clinical development and market authorization of Glybera. (Q37712530)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23808604%20AND%20SRC:MED&resulttype=core&format=json

4 March 2020

title

Lessons learned from the clinical development and market authorization of Glybera (English)

1 reference

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4 March 2020

1 reference

1

1 reference

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4 March 2020

James Wilson

10

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4 March 2020

author name string

Devin M Christopher

2

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4 March 2020

April R Giles

3

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4 March 2020

Christian Hinderer

4

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4 March 2020

Jesse L Rodriguez

5

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4 March 2020

Jenessa B Smith

6

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4 March 2020

Elizabeth A Traxler

7

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4 March 2020

Josh Tycko

8

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4 March 2020

Adam P Wojno

9

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4 March 2020

language of work or name

1 reference

29 June 2013

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:23808604%20AND%20SRC:MED&resulttype=core&format=json

Human gene therapy. Clinical development

4 March 2020

published in

1 reference

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4 March 2020

volume

24

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4 March 2020

page(s)

55-64

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4 March 2020

issue

2

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Efficacy and long-term safety of alipogene tiparvovec (AAV1-LPLS447X) gene therapy for lipoprotein lipase deficiency: an open-label trial

4 March 2020

cites work

1 reference

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The AAV vector toolkit: poised at the clinical crossroads

23 August 2017

1 reference

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Review of the clinical development of alipogene tiparvovec gene therapy for lipoprotein lipase deficiency

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Successful transduction of liver in hemophilia by AAV-Factor IX and limitations imposed by the host immune response

23 August 2017

1 reference

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ADENOVIRUS-ASSOCIATED DEFECTIVE VIRUS PARTICLES

23 August 2017

1 reference

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Induction of immune tolerance to coagulation factor IX antigen by in vivo hepatic gene transfer

23 August 2017

1 reference

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Issues in hyperlipidemic pancreatitis

23 August 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Lipoprotein lipase: structure, function, regulation, and role in disease

23 August 2017

1 reference

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Nucleotide sequence of human cDNA coding for a lipoprotein lipase (LPL) cloned from placental cDNA library

23 August 2017

1 reference

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Gene therapy vectors based on adeno-associated virus type 1.

23 August 2017

1 reference

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From mutation identification to therapy: discovery and origins of the first approved gene therapy in the Western world

14 September 2017

1 reference

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Intramuscular administration of AAV1-lipoprotein lipase S447X lowers triglycerides in lipoprotein lipase-deficient patients

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Correction of feline lipoprotein lipase deficiency with adeno-associated virus serotype 1-mediated gene transfer of the lipoprotein lipase S447X beneficial mutation

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Gene therapy for lipoprotein lipase deficiency: working toward clinical application

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Complete rescue of lipoprotein lipase-deficient mice by somatic gene transfer of the naturally occurring LPLS447X beneficial mutation

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

Long-term correction of murine lipoprotein lipase deficiency with AAV1-mediated gene transfer of the naturally occurring LPL(S447X) beneficial mutation

1 September 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=3992977

1 September 2018

1 reference

https://pubmed.ncbi.nlm.nih.gov/23808604

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Effect of alipogene tiparvovec (AAV1-LPL(S447X)) on postprandial chylomicron metabolism in lipoprotein lipase-deficient patients

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/23808604

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1089/HUMC.2013.087

1 reference

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4 March 2020

1 reference

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4 March 2020

1 reference