RNA repair restores hemoglobin expression in IVS2-654 thalassemic mice (Q37079038)

18 August 2017

RNA repair restores hemoglobin expression in IVS2-654 thalassemic mice (English)

1 reference

18 August 2017

7

Oliver Smithies

1 reference

18 August 2017

8

Ryszard Kole

1 reference

18 August 2017

Saovaros Svasti

1

1 reference

18 August 2017

Thipparat Suwanmanee

2

1 reference

18 August 2017

Suthat Fucharoen

3

1 reference

18 August 2017

Hong M Moulton

4

1 reference

18 August 2017

Michelle H Nelson

5

1 reference

18 August 2017

Nobuyo Maeda

6

1 reference

18 August 2017

language of work or name

English

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publication date

21 January 2009

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Proceedings of the National Academy of Sciences of the United States of America

18 August 2017

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18 August 2017

106

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18 August 2017

1205-1210

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18 August 2017

4

1 reference

describes a project that uses

18 August 2017

ImageQuant

1 reference

11 June 2022

https://www.ebi.ac.uk/europepmc/webservices/rest/PMC2633555/fullTextXML

inferred from PubMed Central ID database lookup

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An endogenous TNF-alpha antagonist induced by splice-switching oligonucleotides reduces inflammation in hepatitis and arthritis mouse models

29 September 2017

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Repair of a splicing defect in erythroid cells from patients with beta-thalassemia/HbE disorder

29 September 2017

1 reference

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Restoration of human beta-globin gene expression in murine and human IVS2-654 thalassemic erythroid cells by free uptake of antisense oligonucleotides.

29 September 2017

1 reference

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Control of alternative splicing by antisense oligonucleotides as a potential chemotherapy: effects on gene expression

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29 September 2017

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Restoration of hemoglobin A synthesis in erythroid cells from peripheral blood of thalassemic patients

29 September 2017

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Specific removal of the nonsense mutation from the mdx dystrophin mRNA using antisense oligonucleotides.

29 September 2017

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29 September 2017

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Up-regulation of luciferase gene expression with antisense oligonucleotides: implications and applications in functional assay development

29 September 2017

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29 September 2017

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Repair of thalassemic human beta-globin mRNA in mammalian cells by antisense oligonucleotides

29 September 2017

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Restoration of correct splicing in thalassemic pre-mRNA by antisense oligonucleotides

29 September 2017

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Systemically delivered antisense oligomers upregulate gene expression in mouse tissues

29 September 2017

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Hemoglobinopathies in Southeast Asia: molecular biology and clinical medicine

27 June 2018

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Systemic delivery of morpholino oligonucleotide restores dystrophin expression bodywide and improves dystrophic pathology

27 June 2018

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4 September 2018

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Comparison of mechanisms of anemia in mice with sickle cell disease and beta-thalassemia: peripheral destruction, ineffective erythropoiesis, and phospholipid scramblase-mediated phosphatidylserine exposure

4 September 2018

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Bone marrow transplantation in adult thalassemic patients

4 September 2018

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https://pubmed.ncbi.nlm.nih.gov/19164558

12 December 2020

inferred from PubMed ID database lookup

Efficient and persistent splice switching by systemically delivered LNA oligonucleotides in mice

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19164558

12 December 2020

inferred from PubMed ID database lookup

An Endogenous TNF-α Antagonist Induced by Splice-switching Oligonucleotides Reduces Inflammation in Hepatitis and Arthritis Mouse Models

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19164558

12 December 2020

inferred from PubMed ID database lookup

Identifiers

DOI

10.1073/PNAS.0812436106

1 reference

18 August 2017

0 references

1 reference

18 August 2017

1 reference