Disease and patient characteristics in NP-C patients: findings from an international disease registry (Q36572002)

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scientific article published on 16 January 2013
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Disease and patient characteristics in NP-C patients: findings from an international disease registry
scientific article published on 16 January 2013

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    Disease and patient characteristics in NP-C patients: findings from an international disease registry (English)
    Marc C Patterson
    Frits A Wijburg
    Audrey Muller
    Barbara Schwierin
    Harir Drevon
    Marie T Vanier
    Mercé Pineda
    16 January 2013

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