Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial (Q35078437)
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| Language | Label | Description | Also known as |
|---|---|---|---|
| English | Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial |
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Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial (English)
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Paul E Monahan
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Junjiang Sun
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Tong Gui
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Genlin Hu
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William B Hannah
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David G Wichlan
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Zhijian Wu
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Joshua C Grieger
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Chengwen Li
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Thipparat Suwanmanee
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Darrel W Stafford
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Carmen J Booth
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Jade J Samulski
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Tal Kafri
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Scott W J McPhee
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R Jude Samulski
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21 January 2015
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