Improved antisense oligonucleotide design to suppress aberrant SMN2 gene transcript processing: towards a treatment for spinal muscular atrophy (Q34695728)
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English | Improved antisense oligonucleotide design to suppress aberrant SMN2 gene transcript processing: towards a treatment for spinal muscular atrophy |
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Improved antisense oligonucleotide design to suppress aberrant SMN2 gene transcript processing: towards a treatment for spinal muscular atrophy (English)
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Chalermchai Mitrpant
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Paul Porensky
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Haiyan Zhou
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Loren Price
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Francesco Muntoni
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Sue Fletcher
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Steve D Wilton
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Arthur H M Burghes
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22 April 2013
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22 April 2013
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