Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model. (Q34574529)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16501048%20AND%20SRC:MED&resulttype=core&format=json

17 January 2020

title

Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model (English)

1 reference

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Duchenne muscular dystrophy

17 January 2020

main subject

gene therapy

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1

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17 January 2020

Alessandro Rosa

2

1 reference

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17 January 2020

Giuseppe D'Antona

3

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17 January 2020

Carmine Nicoletti

6

1 reference

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17 January 2020

Valeria Parente

9

1 reference

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17 January 2020

Antonio Musarò

10

1 reference

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17 January 2020

Alberto Auricchio

11

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17 January 2020

7

Mariacarmela Allocca

1 reference

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17 January 2020

author name string

Olga Sthandier

4

1 reference

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17 January 2020

Fernanda Gabriella De Angelis

5

1 reference

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17 January 2020

Orietta Pansarasa

8

1 reference

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17 January 2020

Roberto Bottinelli

12

1 reference

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17 January 2020

Irene Bozzoni

13

1 reference

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17 January 2020

language of work or name

English

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publication date

24 February 2006

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16501048%20AND%20SRC:MED&resulttype=core&format=json

Proceedings of the National Academy of Sciences of the United States of America

17 January 2020

published in

1 reference

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17 January 2020

volume

103

1 reference

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17 January 2020

issue

10

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17 January 2020

page(s)

3758-3763

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Systemic delivery of antisense oligoribonucleotide restores dystrophin expression in body-wide skeletal muscles

17 January 2020

cites work

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Human circulating AC133(+) stem cells restore dystrophin expression and ameliorate function in dystrophic skeletal muscle

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Antisense-induced multiexon skipping for Duchenne muscular dystrophy makes more sense

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Advances in Duchenne muscular dystrophy gene therapy

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Cell Therapy of -Sarcoglycan Null Dystrophic Mice Through Intra-Arterial Delivery of Mesoangioblasts

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

U7 snRNAs induce correction of mutated dystrophin pre-mRNA by exon skipping

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Functional correction of adult mdx mouse muscle using gutted adenoviral vectors expressing full-length dystrophin.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Chimeric snRNA molecules carrying antisense sequences against the splice junctions of exon 51 of the dystrophin pre-mRNA induce exon skipping and restoration of a dystrophin synthesis in Delta 48-50 DMD cells

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Antisense-induced exon skipping and synthesis of dystrophin in the mdx mouse

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Adeno-associated virus vector carrying human minidystrophin genes effectively ameliorates muscular dystrophy in mdx mouse model

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Inhibition of human immunodeficiency virus type 1 replication by nuclear chimeric anti-HIV ribozymes in a human T lymphoblastoid cell line

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

The molecular basis for Duchenne versus Becker muscular dystrophy: correlation of severity with type of deletion

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=1450150

Adeno-associated virus serotype 8 efficiently delivers genes to muscle and heart

7 July 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Functional amounts of dystrophin produced by skipping the mutated exon in the mdx dystrophic mouse

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Targeted exon skipping in transgenic hDMD mice: A model for direct preclinical screening of human-specific antisense oligonucleotides

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Exchange of surface proteins impacts on viral vector cellular specificity and transduction characteristics: the retina as a model

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Human circulating AC133+ stem cells restore dystrophin expression and ameliorate function in dystrophic skeletal muscle

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Long-term pharmacologically regulated expression of erythropoietin in primates following AAV-mediated gene transfer.

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

The effect of ageing and immobilization on structure and function of human skeletal muscle fibres.

21 January 2018

1 reference

https://api.crossref.org/works/10.1073%2FPNAS.0508917103

Sustained muscle expression of dystrophin from a high-capacity adenoviral vector with systemic gene transfer of T cell costimulatory blockade

21 January 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/16501048

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

The molecular basis of muscular dystrophy in the mdx mouse: a point mutation

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/16501048

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Force-velocity properties of human skeletal muscle fibres: myosin heavy chain isoform and temperature dependence

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/16501048

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1073/PNAS.0508917103

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16501048%20AND%20SRC:MED&resulttype=core&format=json

17 January 2020

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:16501048%20AND%20SRC:MED&resulttype=core&format=json

17 January 2020

1 reference