Gene therapy for genetic haematological disorders and immunodeficiencies (Q34216698)

31 July 2017

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title

Gene therapy for genetic haematological disorders and immunodeficiencies (English)

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31 July 2017

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1

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PubMed ID

11298858

31 July 2017

language of work or name

English

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publication date

1 April 2001

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Journal of Internal Medicine

31 July 2017

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31 July 2017

249

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31 July 2017

4

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31 July 2017

379-390

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Gene transfer to hematopoietic stem cells: implications for gene therapy of human disease.

31 July 2017

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Transduction of human CD34+ cells that mediate long-term engraftment of NOD/SCID mice by HIV vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Stable transduction of quiescent CD34(+)CD38(-) human hematopoietic cells by HIV-1-based lentiviral vectors

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Retrovirus-mediated transfer of the human alpha-L-iduronidase cDNA into human hematopoietic progenitor cells leads to correction in trans of Hurler fibroblasts

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

A chromatin insulator protects retrovirus vectors from chromosomal position effects

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Preselection of retrovirally transduced bone marrow avoids subsequent stem cell gene silencing and age-dependent extinction of expression of human beta-globin in engrafted mice.

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Long-term cure of the photosensitivity of murine erythropoietic protoporphyria by preselective gene therapy

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Gene therapy for adenosine deaminase deficiency

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Gene therapy of human severe combined immunodeficiency (SCID)-X1 disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Genetic, biochemical, and clinical features of chronic granulomatous disease.

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Prolonged production of NADPH oxidase-corrected granulocytes after gene therapy of chronic granulomatous disease

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Retroviral transfer of the glucocerebrosidase gene into CD34+ cells from patients with Gaucher disease: in vivo detection of transduced cells without myeloablation

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Engraftment of hematopoietic progenitor cells transduced with the Fanconi anemia group C gene (FANCC)

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Therapeutic haemoglobin synthesis in beta-thalassaemic mice expressing lentivirus-encoded human beta-globin

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

Prolonged high-level detection of retrovirally marked hematopoietic cells in nonhuman primates after transduction of CD34+ progenitors using clinically feasible methods

21 January 2018

1 reference

https://api.crossref.org/works/10.1046%2FJ.1365-2796.2001.00803.X

10.1046/J.1365-2796.2001.00803.X

21 January 2018

Identifiers

DOI

1 reference

31 July 2017

1 reference

PubMed ID

11298858