A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new ground (Q33950888)

30 July 2017

1 reference

title

A renaissance for antisense oligonucleotide drugs in neurology: exon skipping breaks new ground (English)

1 reference

30 July 2017

6

Eric P Hoffman

1 reference

30 July 2017

Toshifumi Yokota

1

1 reference

30 July 2017

Shin'ichi Takeda

2

1 reference

30 July 2017

Qi-Long Lu

3

1 reference

30 July 2017

Terence A Partridge

4

1 reference

30 July 2017

Akinori Nakamura

5

1 reference

30 July 2017

1 January 2009

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30 July 2017

Archives of Neurology

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30 July 2017

66

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30 July 2017

1

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30 July 2017

32-38

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Optimizing exon skipping therapies for DMD.

30 July 2017

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Follow-up of three patients with a large in-frame deletion of exons 45-55 in the Duchenne muscular dystrophy (DMD) gene

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Correction of ClC-1 splicing eliminates chloride channelopathy and myotonia in mouse models of myotonic dystrophy

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Inhibition of HIV-1 multiplication by a modified U7 snRNA inducing Tat and Rev exon skipping

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Enhancement of SMN2 exon 7 inclusion by antisense oligonucleotides targeting the exon

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Hybrid spectrin type repeats produced by exon-skipping in dystrophin

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Gene-specific countermeasures against Ebola virus based on antisense phosphorodiamidate morpholino oligomers.

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Short interfering RNA confers intracellular antiviral immunity in human cells

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Antisense RNA: function and fate of duplex RNA in cells of higher eukaryotes.

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Modification of splicing in the dystrophin gene in cultured Mdx muscle cells by antisense oligoribonucleotides

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Bidirectional Transcription and the Regulation of Phage λ Repressor Synthesis

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Dystrophin: the protein product of the Duchenne muscular dystrophy locus

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Stable reduction of thymidine kinase activity in cells expressing high levels of anti-sense RNA.

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Genotype-phenotype correlation and germline mosaicism in DMD/BMD patients with deletions of the dystrophin gene

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Integrated DNA, cDNA, and protein studies in Becker muscular dystrophy show high exception to the reading frame rule

5 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Duchenne and Becker muscular dystrophies: an Estonian experience.

29 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=4111150

Multiexon skipping leading to an artificial DMD protein lacking amino acids from exons 45 through 55 could rescue up to 63% of patients with Duchenne muscular dystrophy

29 October 2018

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19139297

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Local dystrophin restoration with antisense oligonucleotide PRO051

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19139297

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Skipping toward personalized molecular medicine

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/19139297

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1001/ARCHNEUROL.2008.540

1 reference

30 July 2017

1 reference

30 July 2017

1 reference