Immune responses and hypercoagulation in ERT for Pompe disease are mutation and rhGAA dose dependent. (Q33711395)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24897114%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

title

Immune responses and hypercoagulation in ERT for Pompe disease are mutation and rhGAA dose dependent (English)

1 reference

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19 March 2020

1

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19 March 2020

Phillip A Doerfler

2

1 reference

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19 March 2020

author name string

Stacy L Porvasnik

3

1 reference

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19 March 2020

Denise D Cloutier

4

1 reference

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19 March 2020

Richie Khanna

5

1 reference

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19 March 2020

Ken J Valenzano

6

1 reference

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19 March 2020

Roland W Herzog

7

1 reference

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19 March 2020

Barry J Byrne

8

1 reference

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19 March 2020

language of work or name

English

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publication date

4 June 2014

1 reference

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19 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24897114%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

volume

9

1 reference

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19 March 2020

issue

6

1 reference

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19 March 2020

page(s)

e98336

1 reference

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Creative Commons Attribution 4.0 International

19 March 2020

copyright license

start time

4 June 2014

1 reference

April 2022 Public Data File from Crossref

copyright status

copyrighted

0 references

cites work

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B-Cell depletion and immunomodulation before initiation of enzyme replacement therapy blocks the immune response to acid alpha-glucosidase in infantile-onset Pompe disease.

21 June 2018

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Glycosylation-independent lysosomal targeting of acid α-glucosidase enhances muscle glycogen clearance in pompe mice

21 June 2018

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Bortezomib in the rapid reduction of high sustained antibody titers in disorders treated with therapeutic protein: lessons learned from Pompe disease

21 June 2018

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Long-term clinical outcomes in type 1 Gaucher disease following 10 years of imiglucerase treatment

21 June 2018

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The pharmacological chaperone AT2220 increases recombinant human acid α-glucosidase uptake and glycogen reduction in a mouse model of Pompe disease

21 June 2018

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Viral acute lower respiratory infections impair CD8+ T cells through PD-1

21 June 2018

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Mapping the T helper cell response to acid α-glucosidase in Pompe mice

21 June 2018

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36 months observational clinical study of 38 adult Pompe disease patients under alglucosidase alfa enzyme replacement therapy

21 June 2018

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The role of immune tolerance induction in restoration of the efficacy of ERT in Pompe disease

21 June 2018

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Successful immune tolerance induction to enzyme replacement therapy in CRIM-negative infantile Pompe disease.

21 June 2018

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Identification and characterization of pharmacological chaperones to correct enzyme deficiencies in lysosomal storage disorders

21 June 2018

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21 June 2018

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Differential pathogenesis of respiratory syncytial virus clinical isolates in BALB/c mice

21 June 2018

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Sphingosine kinase 1 and sphingosine-1-phosphate receptor 2 are vital to recovery from anaphylactic shock in mice.

21 June 2018

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Oral delivery of bioencapsulated coagulation factor IX prevents inhibitor formation and fatal anaphylaxis in hemophilia B mice

21 June 2018

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Cross-reactive immunologic material status affects treatment outcomes in Pompe disease infants

21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 June 2018

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21 January 2018

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Evasion of immune responses to introduced human acid alpha-glucosidase by liver-restricted expression in glycogen storage disease type II.

21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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21 January 2018

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PubMed

https://pubmed.ncbi.nlm.nih.gov/24897114

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

High antibody titer in an adult with Pompe disease affects treatment with alglucosidase alfa

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/24897114

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Systemic anaphylaxis--separation of cardiac reactions from respiratory and peripheral vascular events

1 reference

PubMed

https://pubmed.ncbi.nlm.nih.gov/24897114

inferred from PubMed ID database lookup

12 December 2020

based on heuristic

Identifiers

DOI

10.1371/JOURNAL.PONE.0098336

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24897114%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

0 references

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24897114%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:24897114%20AND%20SRC:MED&resulttype=core&format=json