Curative ex vivo liver-directed gene therapy in a pig model of hereditary tyrosinemia type 1. (Q30856034)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:27464750%20AND%20SRC:MED&resulttype=core&format=json

19 March 2020

title

Curative ex vivo liver-directed gene therapy in a pig model of hereditary tyrosinemia type 1 (English)

1 reference

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19 March 2020

0 references

9

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19 March 2020

Markus Grompe

18

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19 March 2020

21

Stephen J Russell

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19 March 2020

15

Kah Whye Peng

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19 March 2020

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Lukkana Suksanpaisan

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19 March 2020

2

Shennen A Mao

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19 March 2020

3

Jaime Glorioso

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19 March 2020

5

Bruce Amiot

1 reference

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19 March 2020

10

Timothy R DeGrado

1 reference

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19 March 2020

22

Scott L Nyberg

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19 March 2020

author name string

Raymond D Hickey

1

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19 March 2020

Faysal Elgilani

4

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19 March 2020

Harvey Chen

6

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19 March 2020

Piero Rinaldo

7

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19 March 2020

Ronald Marler

8

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19 March 2020

Michael K O'Connor

12

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19 March 2020

Brittany L Freeman

13

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19 March 2020

Samar H Ibrahim

14

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19 March 2020

Cary O Harding

16

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19 March 2020

Chak-Sum Ho

17

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19 March 2020

Yasuhiro Ikeda

19

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19 March 2020

Joseph B Lillegard

20

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19 March 2020

language of work or name

English

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publication date

1 July 2016

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Science Translational Medicine

19 March 2020

published in

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19 March 2020

volume

8

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19 March 2020

page(s)

349ra99

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19 March 2020

issue

349

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Liver-directed lentiviral gene therapy in a dog model of hemophilia B.

19 March 2020

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28 July 2018

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21 January 2018

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12 December 2020

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Identifiers

DOI

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19 March 2020

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19 March 2020

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