Gene editing in human stem cells using zinc finger nucleases and integrase-defective lentiviral vector delivery (Q29014419)

23 March 2017

author

Angelo Leone Lombardo

1

Angelo Lombardo

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12

Luigi Naldini

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Pietro Genovese

Pietro Genovese

2

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Philip D Gregory

Philip D Gregory

10

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Silvia Colleoni

4

Silvia Colleoni

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23 March 2017

8

Fyodor D Urnov

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23 March 2017

author name string

Christian M Beausejour

3

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23 March 2017

Ya-Li Lee

5

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23 March 2017

Kenneth A Kim

6

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23 March 2017

Dale Ando

7

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23 March 2017

Cesare Galli

9

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23 March 2017

Michael C Holmes

11

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23 March 2017

publication date

28 October 2007

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23 March 2017

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23 March 2017

volume

25

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23 March 2017

page(s)

1298-1306

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23 March 2017

issue

11

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Gene conversion tracts from double-strand break repair in mammalian cells

23 March 2017

cites work

1 reference

Generating mice with targeted mutations

21 January 2018

1 reference

7 January 2021

Gene conversion: mechanisms, evolution and human disease

1 reference

7 January 2021

Gene correction in hematopoietic progenitor cells by homologous recombination

1 reference

7 January 2021

Homologous recombination in human embryonic stem cells.

1 reference

7 January 2021

1 reference

7 January 2021

Forty years with homologous recombination.

1 reference

7 January 2021

Gene targeting with viral vectors

1 reference

7 January 2021

Chance or necessity? Insertional mutagenesis in gene therapy and its consequences

1 reference

7 January 2021

Genome-wide analysis of retroviral DNA integration

1 reference

7 January 2021

Hematopoietic stem cell gene transfer in a tumor-prone mouse model uncovers low genotoxicity of lentiviral vector integration

1 reference

7 January 2021

Genotoxicity of retroviral integration in hematopoietic cells.

1 reference

7 January 2021

Correction of ADA-SCID by stem cell gene therapy combined with nonmyeloablative conditioning

1 reference

7 January 2021

Gene therapy of X-linked severe combined immunodeficiency by use of a pseudotyped gammaretroviral vector

1 reference

7 January 2021

Gene therapy for severe combined immunodeficiency

1 reference

7 January 2021

Correction of X-linked chronic granulomatous disease by gene therapy, augmented by insertional activation of MDS1-EVI1, PRDM16 or SETBP1.

1 reference

7 January 2021

LMO2-associated clonal T cell proliferation in two patients after gene therapy for SCID-X1

1 reference

7 January 2021

Gene therapy: therapeutic gene causing lymphoma

1 reference

7 January 2021

Gene therapy: X-SCID transgene leukaemogenicity

1 reference

7 January 2021

Rescue of dystrophic muscle through U7 snRNA-mediated exon skipping

1 reference

7 January 2021

Trans-splicing repair of CD40 ligand deficiency results in naturally regulated correction of a mouse model of hyper-IgM X-linked immunodeficiency.

1 reference

7 January 2021

Gene targeting in stem cells from individuals with osteogenesis imperfecta

1 reference

7 January 2021

Gene targeting in vivo by adeno-associated virus vectors.

1 reference

7 January 2021

The phiC31 integrase system for gene therapy

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7 January 2021

Gene targeting using zinc finger nucleases

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7 January 2021

Chimeric nucleases stimulate gene targeting in human cells

1 reference

7 January 2021

Stimulation of homologous recombination through targeted cleavage by chimeric nucleases

1 reference

7 January 2021

Design and selection of novel Cys2His2 zinc finger proteins

1 reference

7 January 2021

Zinc-finger protein-targeted gene regulation: genomewide single-gene specificity.

1 reference

7 January 2021

Hybrid restriction enzymes: zinc finger fusions to Fok I cleavage domain

1 reference

7 January 2021

FokI dimerization is required for DNA cleavage

1 reference

7 January 2021

The role of double-strand break repair — insights from human genetics

1 reference

7 January 2021

Highly efficient endogenous human gene correction using designed zinc-finger nucleases

1 reference

7 January 2021

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

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7 January 2021

Novel integrase-defective lentiviral episomal vectors for gene transfer

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7 January 2021

Transient gene expression by nonintegrating lentiviral vectors

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7 January 2021

Effective gene therapy with nonintegrating lentiviral vectors

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7 January 2021

Lentiviral vectors with a defective integrase allow efficient and sustained transgene expression in vitro and in vivo

1 reference

7 January 2021

Molecular defects in human severe combined immunodeficiency and approaches to immune reconstitution

1 reference

7 January 2021

CCR5: no longer a "good for nothing" gene--chemokine control of West Nile virus infection

1 reference

7 January 2021

Derivation of Embryonic Stem-Cell Lines from Human Blastocysts

1 reference

7 January 2021

Human immunodeficiency virus type 1 incorporated with fusion proteins consisting of integrase and the designed polydactyl zinc finger protein E2C can bias integration of viral DNA into a predetermined chromosomal region in human cells

1 reference

7 January 2021

Modulating target site selection during human immunodeficiency virus DNA integration in vitro with an engineered tethering factor

1 reference

7 January 2021

Complementation of integrase function in HIV-1 virions.

1 reference

7 January 2021

Mechanism of homologous recombination: mediators and helicases take on regulatory functions

1 reference

7 January 2021

Identification and analysis of functional elements in 1% of the human genome by the ENCODE pilot project

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7 January 2021

An improved zinc-finger nuclease architecture for highly specific genome editing

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7 January 2021

Proteasome activity restricts lentiviral gene transfer into hematopoietic stem cells and is down-regulated by cytokines that enhance transduction.

1 reference

7 January 2021

[26] Generation of HIV-1 derived lentiviral vectors

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7 January 2021

Endogenous microRNA regulation suppresses transgene expression in hematopoietic lineages and enables stable gene transfer

1 reference

7 January 2021

Identifiers

DOI

10.1038/NBT1353

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23 March 2017

Consolidated OpenCitations Corpus – April 2017

Dimensions Publication ID

233707

1026122095

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233707

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Consolidated OpenCitations Corpus – April 2017

Consolidated OpenCitations Corpus – April 2017

1 reference