Long-term safety and efficacy of enzyme replacement therapy for Fabry disease (Q24533551)
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English | Long-term safety and efficacy of enzyme replacement therapy for Fabry disease |
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Long-term safety and efficacy of enzyme replacement therapy for Fabry disease (English)
Robert J Desnick
Gabor E Linthorst
William R Wilcox
Maryam Banikazemi
Nathalie Guffon
Stephen Waldek
Philip Lee
International Fabry Disease Study Group
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